“Patient Voice – Join us in making the voice of rare diseases heard.” This is the theme of Rare Disease Day 2016 – and a cause for Actelion to emphasize its long-term commitment to support the needs of the patient community.

ALLSCHWIL, SWITZERLAND – 29 February 2016 – Today, on Rare Disease Day 2016, patients, their families and caregivers, patient organizations, medical professionals, politicians and researchers are coming together to raise awareness for what living with a rare disease means for those affected and for their families.

Patients play a crucial role in bringing both research and the standard of care in rare diseases forward, which is recognized in the theme of this year’s Rare Disease Day, ‘Patient Voice’.  For Actelion, listening to patients’ voices and working closely with the rare disease community is key to delivering on the company’s mission to discover new innovative drugs for rare diseases and to help more patients with groundbreaking therapies. At the end of 2015, over 65,000 patients were benefiting from Actelion’s rare disease drugs, and the company continues to work with governments and other stakeholders to widen accessibility around the world.

On February 23 in Brussels, our commitment to rare diseases was publicly recognized by the European Organization for Rare Diseases (EURORDIS) as Actelion was honored with the EURORDIS Company Award 2016. Presented to pioneering companies for the development of treatments for rare diseases, the award in particular acknowledges Actelion’s work with patient groups to support the patient and carer community.

Through the company’s collaborative work with patient groups and healthcare professionals, Actelion has become a trusted partner in supporting activities that raise awareness of the challenges facing those living with rare diseases and help bring about positive change. Activities include the development of educational resources such as the innovative PAHuman® eBook to better explain the disease and its impact, and the “Think Again. Think NP-C” campaign to encourage earlier diagnosis of Niemann-Pick type C disease among healthcare professionals unfamiliar with this rare condition.

Gerald Fischer, CEO of the European Pulmonary Hypertension Association (PHA Europe), said: “Actelion has provided invaluable support to our activities and, as a result, our collaboration has led to many great achievements over the years. It’s clear that Actelion’s commitment extends beyond the discovery and development of new medicines and includes initiatives that increase knowledge and understanding of PAH and other rare diseases, which is crucial to organizations like ours.”

An example of Actelion’s pioneering work in rare diseases is an ongoing clinical study involving patients with Eisenmenger syndrome. Working with ethics committees, patient advocacy, support groups and patients’ families, Actelion has extended the study on Eisenmenger syndrome to Down syndrome patients, which will help to address the high unmet medical need for effective, targeted PAH therapies in this vulnerable and too rarely considered population.

Martine Clozel, MD, Chief Scientific Officer at Actelion, commented: “I am very proud that, together with the PAH community, Actelion has brought about not one, but several paradigm shifts in PAH care. The three established pathways in PAH are now well served, but our discovery efforts continue. We are turning to new pathways in PAH, helped by our strong connections with academia, to further improve the prognosis for patients living with this devastating disease. Actelion also plays a leadership role in Niemann-Pick type C disease, where the lives of many patients have been positively impacted. I am convinced that with our strong and innovative research, Actelion will continue to advance care in many rare diseases.”

Source: https://www.actelion.com/en/our-company/news-and-events.page?newsId=1989999

As a custom essay writing, we are in a position to execute any type of written assignment. If you happen to will need methodology format guide by way of example for your research paper, we


As a custom essay writing, we’re in a position to carry out any kind of written assignment. If you ever need to have methodology format assistance for instance for the research paper, we will be able to make it easier to with that. Methodology itself isn’t tight to a distinct topic or project. As you understand the analysis could be performed in any study. You are becoming directed by the thesis subjects for discussions that you are offered. Commonly, your study curriculum will offer you using a format of analysis proposal that could enable you to to guide your own methodology. Buy custom essays from us and get the good quality writing now. Methodology could be the analysis of certain principals of some solutions. It could also be an analysis of guidelines, laws, postulates which are utilized by any type of discipline.

Methodology doesnt describe anything, but is able to show a framework. It may also describe a process of theories and conceptual concepts.

Methodology format aids you to observe some rules and recommendations of a discipline and it is referred to a specific methodology. Every single specialist or professional writer will stick to these rules. MLA and APA methodology are prescribed to become followed when performing a study in subjects of social sciences and humanities. It assists to create a research proposal. You are offered a question thought that’s posed for the audience. You acquire a framework of investigation queries that you simply will answer and get specific final results.

Interesting reality about methodology that it does not have any particular format, however, you have to make an appeal towards the senses of the audience. Collect and present the facts and let readers know how you got it. Details gathering is sampling opinion, undertaking tests, meeting with individuals, and so forth. All of the data must appeal logically, emotionally and ethically. Fact of logic is info depending on details; it truly is objective and relevant for the thesis statement. Reality of feelings is accurate to your own beliefs and not biased. Reality of ethe best essay writing websitethics signifies the facts and data represented in a responsible way.

Methodology format itself is concise and simple-to-understand. Take into account which you have all of the powers to achieve your assignment. Give audience the clue which will lead them throughout information collection and evaluation. Manage your info wisely and make sure to adhere to, revise and strengthen the critical aspects of one’s assignments.

Most of our buyers do share oftentimes their life stories. And also our consumers share with us why they are like or need to have to work with our cheap custom essays


Many of our consumers do share oftentimes their life stories. And also our consumers share with us why they are like or require to make use of our cheap custom essays writing services. All of us are human getting. A single of our key motivations is revenue. Though some individuals may well say that other people who’re contemplating cash an excessive amount of could be lacking the spiritual aspect, we agree that all components of our individuality must be balanced. Getting capable to wisely handle your income is very valuable skill for life. You wouldn’t be able to build sturdy career or possess a satisfied and satisfied household in case you are unable to manage your finances. One more part of very good individual finance management is your potential to set objectives and reach them step-by-step.

If we look in to the past, when we have been young and naive in some strategies, we wanted to grow up and to attain lots with a straight forward flick of our fingers. But since it has turned out, it requires time and work to attain our objectives. Many people might possibly ask why? And the answer is easy this will be the guidelines with the game called ??Life’.

Daily we obtain thousands of order requests. We strive for perfection and prefer to share our writing knowledge with others. Right here are a number of helpful hints for your


Every day we get a huge number of order requests. We strive for perfection and like to share our writing information with other individuals. Here are a number of hints for the best essay writing. Bear in mind when you want cheap custom essays, we’re able to do that writing job for you personally. Getting back to valuable writing strategies let’s get started with application assay writing. Its key purpose should be to be different in the other individuals. Get started with powerful individual statement and concentrate on the explanation why you ought to be taken as the a single and only candidate quantity one particular. If you create argumentative essay, then position your self to proving that your viewpoint would be the most appropriate and reasonable. Argumentative essay demands alot more truthful array of arguments and details as opposed to opinions.

When writing a result in and effect essay, retain your concentrate on comprehensive understanding in the term casual chain. This type of essay needs a robust logic of a domino impact or how one particular result in produces a circumstance with many effects. Classification essay needs category organization to be very easily classified. Compare and contrast writing need to show the distinction. It can be important to show and identify comparison points.